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RNA splicing Mouse models CRISPR/Cas9 Lc3 Cell penetrating peptide Cell model Alternative splicing Hypoxia Neuron CTG repeat instability DMPK Brain Cell culture model RNA interference Glucocorticoid-receptor ARN RNA biology Duchenne muscular dystrophy GABA AAV Acetylcholinesterase knockout mouse Humans Dystrophie Myotonique Glial cells CTG repeats In vivo Cardiac muscle Gene editing CTG repeat contractions Gene therapy Dilated cardiomyopathy Oligodendrocytes Fibrosis Glutamate Skeletal muscle Long read sequencing Genotype phenotype correlation Myelin Myotonic dystrophy Quantitative microdialysis Dystrophie myotonique ACETYLCHOLINESTERASE Intermediate filament Glucocorticoids Antisense oligonucleotides Oligodendrocyte Astrocytes Animals Brain dysfunction Myostatin Exercise Motoneuron BIOLOGIE MOLECULAIRE Desmin Mice Dystrophin Autophagy Thérapie génique Transgenic mouse model CRISPRi Trinucleotide repeat expansion Diaphragm Muscular dystrophy Myotonic dystrophy mouse models Central nervous system Myotonic Dystrophy type 1 Dynamin 2 PacBio Knockout Astrocyte Gene Therapy Aging Myotonic Dystrophy Type 1 DM1 Heart failure DMSXL mice Trinucleotide Repeat Expansion Acetylcholinesterase deficiency Cytoskeleton Heart KNOCKOUT MICE Transcriptomics Mouse model Acute coronary syndrome Muscle MBNL Therapy Antisense oligonucleotide Expression Maximal force Centronuclear myopathy CMS Transgenic mouse Myotonic dystrophy type 1 Male GSK3␤ CONGENITAL MYATHENIC SYNDROME PCR Myotonic Dystrophy Exercice