Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies - Université Paris Cité Accéder directement au contenu
Article Dans Une Revue Molecular Therapy - Nucleic Acids Année : 2023

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hal-04087001 , version 1 (02-05-2023)

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Mégane Brusson, Anne Chalumeau, Pierre Martinucci, Oriana Romano, Tristan Felix, et al.. Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies. Molecular Therapy - Nucleic Acids, 2023, 32 (13), pp.229 - 246. ⟨10.1016/j.omtn.2023.03.012⟩. ⟨hal-04087001⟩

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